BioMarin Pharmaceutical Japan K.K.

Product Information : Genetically modified drug for mucopolysaccharidosis Type ⅣA

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Product Information

Genetically modified drug for mucopolysaccharidosis Type ⅣA

VIMIZIM® ​​Intravenous Solution 5mg

VIMIZIM® ​​Intravenous Solution

Vimizim® (elosulfase alfa) is
an enzyme replacement therapy for the treatment of mucopolysaccharidosis IVA (Morquio A syndrome).

VIMIZIM® ​​Intravenous Solution
Generic Name Elosulfase alfa (genetically modified)
Indication Mucopolysaccharidosis IVA
Dosage and Administration Usually, intravenously infuse 2 mg of elosulfase alfa (genetically modified) per kg body weight at a time, once a week.

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